Clinical trials & news
Current
Stanford trial underway
The first ever gene therapy trial for IPEX is currently underway at Stanford Medicine and actively recruiting!
JUL 2024
Hope for IPEX: Jax's Journey
Boy with IPEX treated with gene therapy at Stanford University
JUL 2023
Innovator Spotlight: Dr. Bacchetta
Dr. Bacchetta of Stanford sits with The Scientist to discuss the future of gene therapy for IPEX
FEB 2022
Stanford trial awarded $12M
The generous grant follows a previous $5.5M grant from CIRM to Dr. Bacchetta's team in 2019
NOV 2019
Stanford trial awarded $5.5M
The generous grant was awarded by CIRM, the California Institute for Regenerative Medicine, for Dr. Bacchetta to pursue trial
SPRING 2019
A second chance at life
Young brothers are saved by a team with new approaches to a rare genetic disease
2017
A rare diagnosis: Nick's Journey
STAT1 mutation discovery opens new treatment options for IPEX-like syndrome